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Drug Discovery

Design Therapeutics launches with $45 million for neurological diseases

by Ryan Cross
March 27, 2020 | A version of this story appeared in Volume 98, Issue 12

 

San Diego–based Design Therapeutics has launched with $45 million in series A financing to develop small-molecule drugs that alter gene expression. The start-up plans to treat nucleotide repeat disorders including Friedreich’s ataxia and myotonic dystrophy. Design was cofounded by Pratik Shah, former chairman of Synthorx, and Aseem Ansari, a biochemist who recently left the University of Wisconsin for St. Jude Children’s Research Hospital. The firm has licensed Ansari’s technology from Wisconsin.

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