ERROR 1
ERROR 1
ERROR 2
ERROR 2
ERROR 2
ERROR 2
ERROR 2
Password and Confirm password must match.
If you have an ACS member number, please enter it here so we can link this account to your membership. (optional)
ERROR 2
ACS values your privacy. By submitting your information, you are gaining access to C&EN and subscribing to our weekly newsletter. We use the information you provide to make your reading experience better, and we will never sell your data to third party members.
San Diego–based Design Therapeutics has launched with $45 million in series A financing to develop small-molecule drugs that alter gene expression. The start-up plans to treat nucleotide repeat disorders including Friedreich’s ataxia and myotonic dystrophy. Design was cofounded by Pratik Shah, former chairman of Synthorx, and Aseem Ansari, a biochemist who recently left the University of Wisconsin for St. Jude Children’s Research Hospital. The firm has licensed Ansari’s technology from Wisconsin.
Join the conversation
Contact the reporter
Submit a Letter to the Editor for publication
Engage with us on X